Chinese Journal of Dermatology ›› 2018, Vol. 51 ›› Issue (11): 843-846.doi: 10.3760/cma.j.issn.0412-4030.2018.11.025
Previous Articles Next Articles
Zhi Dalong, Wang Gang
Received:2017-11-16
Revised:2018-01-12
Online:2018-11-16
Published:2018-10-31
Contact:
Wang Gang
E-mail:xjwgang@fmmu.edu.cn
Zhi Dalong, Wang Gang. Application of CRISPR?Cas9 system in related skin diseases and gene therapy[J].Chinese Journal of Dermatology, 2018, 51(11): 843-846.
| ［1］ | Mali P, Aach J, Stranges PB, et al. CAS9 transcriptional activators for target specificity screening and paired nickases for cooperative genome engineering［J］. Nat Biotechnol, 2013,31（9）:833⁃838. doi: 10.1038/nbt.2675.<br /> |
| ［2］ | Hwang WY, Fu Y, Reyon D, et al. Efficient genome editing in zebrafish using a CRISPR⁃Cas system［J］. Nat Biotechnol, 2013,31（3）:227⁃229. doi: 10.1038/nbt.2501.<br /> |
| ［3］ | Li W, Teng F, Li T, et al. Simultaneous generation and germline transmission of multiple gene mutations in rat using CRISPR⁃Cas systems［J］. Nat Biotechnol, 2013,31（8）:684⁃686. doi: 10.1038/nbt.2652.<br /> |
| ［4］ | Yang H, Wang H, Shivalila CS, et al. One⁃step generation of mice carrying reporter and conditional alleles by CRISPR/Cas⁃mediated genome engineering［J］. Cell, 2013,154（6）:1370⁃1379. doi: 10.1016/j.cell.2013.08.022.<br /> |
| ［5］ | Niu Y, Shen B, Cui Y, et al. Generation of gene⁃modified cynomolgus monkey via Cas9/RNA⁃mediated gene targeting in one⁃cell embryos［J］. Cell, 2014,156（4）:836⁃943. doi: 10.1016/j.cell. 2014.01.027.<br /> |
| ［6］ | Ishino Y, Shinagawa H, Makino K, et al. Nucleotide sequence of the iap gene, responsible for alkaline phosphatase isozyme conversion in Escherichia coli, and identification of the gene product［J］. J Bacteriol, 1987,169（12）:5429⁃5433.<br /> |
| ［7］ | Mojica FJ, Díez⁃Villaseñor C, Soria E, et al. Biological significance of a family of regularly spaced repeats in the genomes of Archaea, Bacteria and mitochondria［J］. Mol Microbiol, 2000,36（1）:244⁃246. doi: 10.1046/j.1365⁃2958.2000.01838.x.<br /> |
| ［8］ | Coffey A, Ross RP. Bacteriophage⁃resistance systems in dairy starter strains: molecular analysis to application［J］. Antonie Van Leeuwenhoek, 2002,82（1⁃4）:303⁃321.<br /> |
| ［9］ | Mojica FJ, Díez⁃Villaseñor C, García⁃Martínez J, et al. Intervening sequences of regularly spaced prokaryotic repeats derive from foreign genetic elements［J］. J Mol Evol, 2005,60（2）:174⁃182. doi: 10.1007/s00239⁃004⁃0046⁃3.<br /> |
| ［10］ | Wiedenheft B, Lander GC, Zhou K, et al. Structures of the RNA⁃guided surveillance complex from a bacterial immune system［J］. Nature, 2011,477（7365）:486⁃489. doi: 10.1038/nature10402.<br /> |
| ［11］ | Zhou X, Xin J, Fan N, et al. Generation of CRISPR/Cas9⁃mediated gene⁃targeted pigs via somatic cell nuclear transfer［J］. Cell Mol Life Sci, 2015,72（6）:1175⁃1184. doi: 10.1007/s00018⁃014⁃1744⁃7.<br /> |
| ［12］ | Xie F, Ye L, Chang JC, et al. Seamless gene correction of β⁃thalassemia mutations in patient⁃specific iPSCs using CRISPR/Cas9 and piggyBac［J］. Genome Res, 2014,24（9）:1526⁃1533. doi: 10.1101/gr.173427.114.<br /> |
| ［13］ | Howden SE, Maufort JP, Duffin BM, et al. Simultaneous re⁃programming and gene correction of patient fibroblasts［J］. Stem Cell Reports, 2015,5（6）:1109⁃1118. doi: 10.1016/j.stemcr.2015.10. 009.<br /> |
| ［14］ | Zhen S, Hua L, Takahashi Y, et al. In vitro and in vivo growth suppression of human papillomavirus 16⁃positive cervical cancer cells by CRISPR/Cas9［J］. Biochem Biophys Res Commun, 2014,450（4）:1422⁃1426. doi: 10.1016/j.bbrc.2014.07.014.<br /> |
| ［15］ | Liu X, Zhang Y, Cheng C, et al. CRISPR⁃Cas9⁃mediated multiplex gene editing in CAR⁃T cells［J］. Cell Res, 2017,27（1）:154⁃157. doi: 10.1038/cr.2016.142.<br /> |
| ［16］ | Chen ZH, Yu YP, Zuo ZH, et al. Targeting genomic re⁃arrangements in tumor cells through Cas9⁃mediated insertion of a suicide gene［J］. Nat Biotechnol, 2017,35（6）:543⁃550. doi: 10. 1038/nbt.3843.<br /> |
| ［17］ | Shi J, Zhao Y, Wang K, et al. Cleavage of GSDMD by inflammatory caspases determines pyroptotic cell death［J］. Nature, 2015,526（7575）:660⁃665. doi: 10.1038/nature15514.<br /> |
| ［18］ | Simeonov DR, Gowen BG, Boontanrart M, et al. Discovery of stimulation⁃responsive immune enhancers with CRISPR activation［J］. Nature, 2017,549（7670）:111⁃115. doi: 10.1038/nature23875.<br /> |
| ［19］ | Zhu S, Li W, Liu J, et al. Genome⁃scale deletion screening of human long non⁃coding RNAs using a paired⁃guide RNA CRISPR⁃Cas9 library［J］. Nat Biotechnol, 2016,34（12）:1279⁃1286. doi: 10.1038/nbt.3715.<br /> |
| ［20］ | Manguso RT, Pope HW, Zimmer MD, et al. In vivo CRISPR screening identifies Ptpn2 as a cancer immunotherapy target［J］. Nature, 2017,547（7664）:413⁃418. doi: 10.1038/nature23270.<br /> |
| ［21］ | Hu W, Kaminski R, Yang F, et al. RNA⁃directed gene editing specifically eradicates latent and prevents new HIV⁃1 infection［J］. Proc Natl Acad Sci U S A, 2014,111（31）:11461⁃11466. doi: 10. 1073/pnas.1405186111.<br /> |
| ［22］ | Kaminski R, Bella R, Yin C, et al. Excision of HIV⁃1 DNA by gene editing: a proof⁃of⁃concept in vivo study［J］. Gene Ther, 2016,23（8⁃9）:696. doi: 10.1038/gt.2016.45.<br /> |
| ［23］ | Xu L, Yang H, Gao Y, et al. CRISPR/Cas9⁃mediated CCR5 ablation in human hematopoietic stem/progenitor cells confers HIV⁃1 resistance In vivo［J］. Mol Ther, 2017,25（8）:1782⁃1789. doi: 10.1016/j.ymthe.2017.04.027.<br /> |
| ［24］ | Yin C, Zhang T, Qu X, et al. In vivo excision of HIV⁃1 provirus by saCas9 and multiplex single⁃guide RNAs in animal models［J］. Mol Ther, 2017,25（5）:1168⁃1186. doi: 10.1016/j.ymthe.2017.03. 012.<br /> |
| ［25］ | Zetsche B, Gootenberg JS, Abudayyeh OO, et al. Cpf1 is a single RNA⁃guided endonuclease of a class 2 CRISPR⁃Cas system［J］. Cell, 2015,163（3）:759⁃771. doi: 10.1016/j.cell.2015.09.038.<br /> |
| ［26］ | Ran FA, Cong L, Yan WX, et al. In vivo genome editing using Staphylococcus aureus Cas9［J］. Nature, 2015,520（7546）:186⁃191. doi: 10.1038/nature14299.<br /> |
| ［27］ | Kim E, Koo T, Park SW, et al. In vivo genome editing with a small Cas9 orthologue derived from Campylobacter jejuni［J］. Nat Commun, 2017,8:14500. doi: 10.1038/ncomms14500.<br /> |
| ［28］ | Gaudelli NM, Komor AC, Rees HA, et al. Programmable base editing of A*T to G*C in genomic DNA without DNA cleavage［J］. Nature, 2017,551（7681）:464⁃471. doi: 10.1038/nature24644.<br /> |
| ［29］ | Komor AC, Kim YB, Packer MS, et al. Programmable editing of a target base in genomic DNA without double⁃stranded DNA cleavage［J］. Nature, 2016,533（7603）:420⁃424. doi: 10.1038/nature 17946.<br /> |
| ［30］ | Brouns SJ, Jore MM, Lundgren M, et al. Small CRISPR RNAs guide antiviral defense in prokaryotes［J］. Science, 2008,321（5891）:960⁃964. doi: 10.1126/science.1159689.<br /> |
| ［31］ | Doench JG, Fusi N, Sullender M, et al. Optimized sgRNA design to maximize activity and minimize off⁃target effects of CRISPR⁃Cas9［J］. Nat Biotechnol, 2016,34（2）:184⁃191. doi: 10.1038/nbt.3437.<br /> |
| ［32］ | Ran FA, Hsu PD, Lin CY, et al. Double nicking by RNA⁃guided CRISPR Cas9 for enhanced genome editing specificity［J］. Cell, 2013,154（6）:1380⁃1389. doi: 10.1016/j.cell.2013.08.021.<br /> |
| ［33］ | Kleinstiver BP, Pattanayak V, Prew MS, et al. High⁃fidelity CRISPR⁃Cas9 nucleases with no detectable genome⁃wide off⁃target effects［J］. Nature, 2016,529（7587）:490⁃495. doi: 10.1038/nature16526.<br /> |
| ［34］ | Slaymaker IM, Gao L, Zetsche B, et al. Rationally engineered Cas9 nucleases with improved specificity［J］. Science, 2016,351（6268）:84⁃88. doi: 10.1126/science.aad5227.<br /> |
| ［35］ | Chen JS, Dagdas YS, Kleinstiver BP, et al. Enhanced proofreading governs CRISPR⁃Cas9 targeting accuracy［J］. Nature, 2017,550（7676）:407⁃410. doi: 10.1038/nature24268.<br /> |
| No related articles found! |
|
